Hazlett is worried that this reflects lower sales of Cordarone for ventricular fibrillation and Refacto for hemophilia.
She stressed that the findings don't have any effect on the use of the drug by hemophilia patients.
Think about the impact of increasing coinsurance for someone with cancer or hemophilia.
The company said the majority of sales of the drug are from out-patient prescriptions for hemophilia patients, not hospital use.
Biogen has a hemophilia program that Wall Street may be undervaluing.
Case in point: two new reports looking at off-label use of the hemophilia drug NovoSeven and two soon-to-be-released studies comparing the off-label use of Avastin vs.
For years, researchers have looked for ways of treating genetic diseases like muscular dystrophy, hemophilia and cystic fibrosis by targeting the genetic defects that cause them.
One major player, venture backed-Biovitrum, which first sold shares to the public on the Stockholm Exchange in 2006, develops drugs to treat diseases including hemophilia, glaucoma and diabetes.
The studies in two types of hemophilia both succeeded this fall, and analysts now forecast annual sales of the drugs in the low hundreds of millions of dollars.
Bayer invests in a risky new strategy for treating hemophilia.
The approval comes amid a flurry of research showing broader promise for the approach in a range of disorders, from a rare form of blindness to hemophilia to heart failure.
It led him to a faculty job at Johns Hopkins and then, in 1987, to Bayer, where he brought to market the first hemophilia drug ever to use recombinant DNA technology.
It is approved by the U.S. Food and Drug Administration for patients with certain forms of hemophilia or congenital deficiencies in the protein, for whom it can prevent potentially fatal episodes of bleeding.
Moreover, while the patient base for Duchenne may be too small to spark a billion-dollar drug, the PTC chemical could work against similar underlying gene flaws in other disorders such as cystic fibrosis, hemophilia and spinal muscular atrophy.
Aside from the hemophilia drugs, the company is also expecting data from a drug for amyotrophic lateral sclerosis and there could be an expert panel for its BG-12 multiple sclerosis pill by the end of the year, with approval expected early in 2013.
FORBES: Biogen's New Hemophilia Drug Could Replace Pfizer's Old One
For these kids, suffering from diseases such as hemophilia, sickle cell anemia and cancer, it is a chance to see past the walls of the hospital to what the world might be like if a diagnosis didn't control their every move, if clinics and hospital rooms weren't like second homes.
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