They predicted progress against genetic diseases like cystic fibrosis and Parkinson's disease.
VOA: special.2010.07.20
It might be a plasmid that contains a promoter that works in lung cells and that has the cystic fibrosis gene.
这个质粒带有,可以在肺细胞表达的启动子和正常基因
You could potentially treat cystic fibrosis by providing the correct gene and providing it to all the cells of the lung epithelium.
一种可能的治愈方法是,把正确的基因,导入所有肺上皮细胞
You get cystic fibrosis because one protein that's made by your lung epithelium is not expressed properly.
得囊胞性纤维症的病因是,肺上皮细胞产生的一种蛋白,表达不正常
Cystic fibrosis is a disease that affects many organ systems, but particularly the lung.
囊胞性纤维症可导致多个器官病变,但尤其是肺部
Because of this, because cystic fibrosis is a disease that's caused by a single gene defect, there's been great interest in trying to treat cystic fibrosis with gene therapy.
就是因为如此,就因为囊胞性纤维症,是一种单基因病,人们对于用基因治疗,治愈囊胞性纤维症产生了很大的兴趣
Another example is cystic fibrosis.
另一例是囊胞性纤维症
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