More importantly, though, it adds to the rather small number of human successes with gene therapy.
但更重要的在于这一成果增加了人类基因治疗的微不足道的成功数量。
Investigators evaluated the gene therapy in two mouse models of retinal degenerative disease, as well as cultures of human retinal tissue.
调查评估了在两个视网膜退行性疾病小鼠模型的基因治疗,以及人体视网膜组织的人文研究。
As this trial is the first to treat an eye disease using administration of gene therapy vectors to human retinas, the team have carried out extensive pre-clinical testing.
因为这项试验首次利用基因治疗载体导入人类视网膜进行眼睛治疗,所以该队伍已经进行了大量的临床前试验。
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